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We work to enhance the quality of life for those living with GNE Myopathy by funding critical research focused on treatments and a cure through The International Gene Therapy Development Program (IGTDP) and by advocacy, education and outreach.

We work to enhance the quality of life for those living with GNE Myopathy by funding critical research focused on treatments and a cure through The International Gene Therapy Development Program (IGTDP) and by advocacy, education and outreach.

Our Virtual Learning Library provides recordings of our GNEM Speaker Series events, podcasts, and webinars and is an invaluable resource where you can find answers to many of your questions about GNE Myopathy and the work of NDF.

GNEM Learning Library
What is GNE Myopathy?
Are there treatments for GNE Myopathy?
How does NDF support patients?
Recently Diagnosed?

Our impact at a glance:

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