Neuromuscular Disease Foundation | Information About GNE Myopathy

We work to enhance the quality of life for those living with GNE Myopathy by funding critical research focused on treatments and a cure through The International Gene Therapy Development Program (IGTDP) and by advocacy, education and outreach.

Our Virtual Learning Library provides recordings of our GNEM Speaker Series events, podcasts, and webinars and is an invaluable resource where you can find answers to many of your questions about GNE Myopathy and the work of NDF.

GNEM Learning Library

What is GNE Myopathy?

Are there treatments for GNE Myopathy?

How does NDF support patients?

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Our impact at a glance:

1531

People Served Annually

1275

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$7.3M

Funded in service of GNEM Science & Programs

38

Countries

43

Associated Scientific Advisors

Latest News

Rushabh Desai Talks About the Struggles of Living with Rare Muscular Disease GNEM

THE HIDDEN CHALLENGES FACED BY DISABLED TEACHERS

The Philosophy of Giving: We Talk with Longtime Board Member and Serial Philanthropist David Haverim about Generosity and The Future of NDF

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