News, Articles and Webinars
July 29, 2026 – Understanding Clinical Trials: What to Expect as a Participant
May 2026 – Therapeutic Update in GNE Myopathy by Dr. T. Mozaffar
What is gene therapy?
Human gene therapy seeks to modify or manipulate the expression of a gene or to alter the biological properties of living cells for therapeutic [...]
Seeing Clearly: The State of NDF
On Sunday, April 3rd, 2022, NDF held an important webinar, entitled Seeing Clearly: The State of NDF. More than 35 participants from our global [...]
It’s A Marathon, Not A Sprint – Why Is This Ultra Rare Disease So Difficult to Diagnose?
We Talk to Doctor and GNEM Patient Suleyman Kus, about His Journey to Diagnosis, and What the Medical Community Can Do Better.Doctor Suleyman Kus of [...]
How The NDF Maintains Transparency with Patients & Donors
Running a nonprofit is not for the faint of heart. It requires drive, vision, extra doses of passion, resourcefulness, and impeccable communication skills. It [...]
What Are The Most Common Neuromuscular Diseases?
Let’s start by understanding what is a neuromuscular disease. Neuromuscular diseases affect the function of muscles due to problems with the nerves and muscles [...]
The NDF Welcomes Geoffrey M. Gee, Esq. as Newly Appointed Executive Director
The Neuromuscular Disease Foundation (NDF) announced that its Board of Directors has appointed Geoffrey Gee, Esq. as Executive Director, effective January 1st, 2022. He [...]
Rare Leader: Geoffrey Gee, Executive Director, Neuromuscular Disease Foundation
A recent interview with NDF's new Executive Director Geoffrey Gee by Global Genes. Disease focus: GNE myopathy is a rare, inherited disease that causes [...]
NDF Takes the Lead in Global Race to Develop Gene Therapy Treatment for GNEM
The Neuromuscular Disease Foundation (also known as NDF) has garnered global attention by making notable advancements in their ambitious plan that was announced in [...]
Why Rare Disease Day is So Important to the Neuromuscular Disease Foundation
The Neuromuscular Disease Foundation (NDF) celebrates Rare Disease Day with its mission to improve treatment and opportunity for the 300 million people worldwide living with [...]
Rushabh Desai Talks About the Struggles of Living with Rare Muscular Disease GNEM
By Dana Corddry Imagine living in a culture where the stigma of having a physical disorder were still very much present. Or where society [...]
